What are the epidemiological methods used to evaluate the effectiveness of ERT?
Epidemiologists use a variety of methods to evaluate the effectiveness of ERT, including cohort studies, case-control studies, and randomized controlled trials. These studies assess clinical outcomes, such as symptom improvement, quality of life, and survival rates, in patients receiving ERT compared to those who do not. Data linkage with healthcare databases and registries can also provide valuable insights into long-term outcomes and treatment adherence.
