How Does Sapropterin Dihydrochloride Impact the Epidemiology of PKU?
The introduction of Sapropterin Dihydrochloride has changed the management of PKU, offering an additional therapeutic option. This can potentially improve the quality of life for responsive patients by allowing for a more relaxed dietary regimen. However, its use is limited to those who respond to the medication, which influences the overall impact on the PKU population.
